Tag Archives: Therapy

Awaiting FDA nod, Novartis touts latest data on gene therapy Zolgensma

As Novartis waits for FDA action on its gene therapy Zolgensma, expected this month, the company has rolled out yet another round of data on the spinal muscular atrophy treatment. Novartis’ AveXis, which developed the gene therapy, touted interim data through March 8 from a phase 1 study in Type 2 SMA patients, plus later-stage… Read More »

Hormone Replacement Therapy for Men: Types & More

Hormone Replacement Therapy: Definition When we talk about hormone replacement therapy (HRT) in men, we’re talking about testosterone. A small amount of testosterone is produced in the adrenal glands, but for men the majority of testosterone is produced in the testicles. Testosterone has both physical and psychological benefits.1 Physically, the hormone has several functions for… Read More »

Three years after undergoing gene therapy, his ‘last shot’ hit the target

Brenden was the first patient enrolled in what became a nine-patient, four-center trial that also involved patients at the National Institutes of Health (NIH) in Maryland, the University of California at Los Angeles, and Great Ormond Street Hospital for Children in London. The trial, funded by the NIH and the California Institute for Regenerative Medicine,… Read More »